The cooperative international neuromuscular research group duchenne natural history study—a longitudinal investigation in the era of glucocorticoid therapy: Design of protocol and the methods used
Muscle & Nerve2013Vol. 48(1), pp. 32–54
Citations Over TimeTop 10% of 2013 papers
Craig M. McDonald, Erik Henricson, Richard T. Abresch, Jay J. Han, Diana M. Escolar, Julaine Florence, Tina Duong, Adrienne Arrieta, Paula R. Clemens, Eric P. Hoffman, Avital Cnaan, the Cinrg Investigators
Abstract
Detailed information on the study methodology of the CINRG DMD-NHS lays the groundwork for future analyses of prospective longitudinal natural history data. These data will assist investigators in designing clinical trials of novel therapeutics.
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