Safe, Efficient, and Reproducible Gene Therapy of the Brain in the Dog Models of Sanfilippo and Hurler Syndromes
Molecular Therapy2010Vol. 19(2), pp. 251–259
Citations Over TimeTop 10% of 2010 papers
N. Matthew Ellinwood, Jérôme Ausseil, Nathalie Desmaris, Stéphanie Bigou, Song Liu, Jackie K. Jens, Elizabeth Snella, Eman E.A. Mohammed, Chris Thomson, Sylvie Raoul, Béatrice Joussemet, Françoise Roux, Yan Chérel, Y Lajat, Monique Piraud, Rachid Benchaouir, Stephan Hermening, Harald Petry, Roseline Froissart, Marc Tardieu, Carine Ciron, Philippe Moullier, J. Parkes, Karen L. Kline, Irène Maire, Marie‐Thérèse Vanier, Jean‐Michel Heard, Marie-Anne Colle
Related Papers
- → Mucopolysaccharidosis Type I: Current Treatments, Limitations, and Prospects for Improvement(2021)80 cited
- → 12 year follow up of enzyme-replacement therapy in two siblings with attenuated mucopolysaccharidosis I: the important role of early treatment(2016)63 cited
- → 18‐year follow‐up of enzyme‐replacement therapy in two siblings with attenuated mucopolysaccharidosis I(2022)7 cited
- → Outcome after three years of laronidase enzyme replacement therapy in a patient with Hurler syndrome(2006)23 cited
- → Hurler syndrome: diagnostic journey in an orphan disease - case report(2021)