Minimal clinically important differences in functional motor scores in adults with spinal muscular atrophy
European Journal of Neurology2020Vol. 27(12), pp. 2586–2594
Citations Over TimeTop 11% of 2020 papers
Benjamin Stolte, J Bois, Saskia Bolz, Kathrin Kizina, Andreas Totzeck, Melina Schlag, Christoph Kleinschnitz, Tim Hagenacker
Abstract
Our data provide MCID values for functional motor scores commonly used in adults with SMA in order to distinguish statistical effects from 'real' changes. A complementary systematic consensus process could help to further adjust the MCID values we propose.
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