A Phenotypic Spectrum Between ALS and Health in Patient-Derived Fibroblasts Enables Subgrouping of FUS and Sporadic ALS and Evaluation of ASO Treatment
SSRN Electronic Journal2022
Karl Kumbier, Maike Roth, Zizheng Li, Julia R. Lazzari-Dean, C. Waters, Ping Huang, Vladislav A. Korobeynikov, Hemali Phatnani, Neil A. Shneider, Matthew P. Jacobson, Lani F. Wu, Steven J. Altschuler
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