Aurélie Goyenvalle
Inserm(FR)Université de Versailles Saint-Quentin-en-Yvelines(FR)Université Paris-Saclay(FR)Scientific Centre of Monaco(MC)
Publications by Year
Research Areas
Muscle Physiology and Disorders, RNA Interference and Gene Delivery, CRISPR and Genetic Engineering, Neurogenetic and Muscular Disorders Research, RNA Research and Splicing
Most-Cited Works
- → Rescue of Dystrophic Muscle Through U7 snRNA-Mediated Exon Skipping(2004)474 cited
- → Delivery of oligonucleotide‐based therapeutics: challenges and opportunities(2021)349 cited
- → Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers(2015)307 cited
- → Restoration of Human Dystrophin Following Transplantation of Exon-Skipping-Engineered DMD Patient Stem Cells into Dystrophic Mice(2007)223 cited
- → Delivery is key: lessons learnt from developing splice‐switching antisense therapies(2017)149 cited
- → Muscle Function Recovery in Golden Retriever Muscular Dystrophy After AAV1-U7 Exon Skipping(2012)128 cited