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Alberto Auricchio | doi.page

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Alberto Auricchio

Federico II University Hospital(IT)Telethon Institute Of Genetics And Medicine(IT)Biogen (Italy)(IT)

Publications by Year

Research Areas

Virus-based gene therapy research, Retinal Development and Disorders, CRISPR and Genetic Engineering, Lysosomal Storage Disorders Research, Retinal Diseases and Treatments

Most-Cited Works

→ Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis(2008)2,126 cited
→ Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial(2009)852 cited
→ Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration(2009)551 cited
→ Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial(2016)450 cited
→ Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model(2001)393 cited
→ AAV2 Gene Therapy Readministration in Three Adults with Congenital Blindness(2012)387 cited

→ Three-Year Follow-up after Unilateral Subretinal Delivery of Adeno-Associated Virus in Patients with Leber Congenital Amaurosis Type 2(2013)327 cited

→ Isolation of Highly Infectious and Pure Adeno-Associated Virus Type 2 Vectors with a Single-Step Gravity-Flow Column(2001)295 cited

→ Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice(2008)283 cited

→ Axonal degeneration in paraplegin-deficient mice is associated with abnormal mitochondria and impairment of axonal transport(2004)270 cited