Jayaprakash K. Nair
Alnylam Pharmaceuticals (United States)(US)
Publications by Year
Research Areas
RNA Interference and Gene Delivery, Advanced biosensing and bioanalysis techniques, MicroRNA in disease regulation, DNA and Nucleic Acid Chemistry, Immunotherapy and Immune Responses
Most-Cited Works
- → Multivalent N-Acetylgalactosamine-Conjugated siRNA Localizes in Hepatocytes and Elicits Robust RNAi-Mediated Gene Silencing(2014)1,048 cited
- → An RNAi therapeutic targeting antithrombin to rebalance the coagulation system and promote hemostasis in hemophilia(2015)291 cited
- → Investigating the pharmacodynamic durability of GalNAc–siRNA conjugates(2020)267 cited
- → Impact of enhanced metabolic stability on pharmacokinetics and pharmacodynamics of GalNAc–siRNA conjugates(2017)259 cited
- → Expanding RNAi therapeutics to extrahepatic tissues with lipophilic conjugates(2022)228 cited
- → Shielding of Lipid Nanoparticles for siRNA Delivery: Impact on Physicochemical Properties, Cytokine Induction, and Efficacy(2014)212 cited
- → siRNA Conjugates Carrying Sequentially Assembled Trivalent N-Acetylgalactosamine Linked Through Nucleosides Elicit Robust Gene Silencing In Vivo in Hepatocytes(2015)207 cited
- → Hepatocyte‐Specific Delivery of siRNAs Conjugated to Novel Non‐nucleosidic Trivalent N‐Acetylgalactosamine Elicits Robust Gene Silencing in Vivo(2015)181 cited
- → Evaluation of GalNAc-siRNA Conjugate Activity in Pre-clinical Animal Models with Reduced Asialoglycoprotein Receptor Expression(2017)107 cited
- → The Nonclinical Disposition and Pharmacokinetic/Pharmacodynamic Properties of N-Acetylgalactosamine–Conjugated Small Interfering RNA Are Highly Predictable and Build Confidence in Translation to Human(2021)98 cited