Eric R. Pozsgai
Sarepta Therapeutics (United States)(US)
Publications by Year
Research Areas
Muscle Physiology and Disorders, Virus-based gene therapy research, Genetic Neurodegenerative Diseases, CAR-T cell therapy research, Neurogenetic and Muscular Disorders Research
Most-Cited Works
- → Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy(2020)377 cited
- → Defective membrane fusion and repair inAnoctamin5-deficient muscular dystrophy(2016)107 cited
- → AAV.Dysferlin Overlap Vectors Restore Function in Dysferlinopathy Animal Models(2015)96 cited
- → Systemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy(2017)86 cited
- → Systemic AAV-Mediated β-Sarcoglycan Delivery Targeting Cardiac and Skeletal Muscle Ameliorates Histological and Functional Deficits in LGMD2E Mice(2017)79 cited
- → Modified mariner Transposons for Random Inducible-Expression Insertions and Transcriptional Reporter Fusion Insertions in Bacillus subtilis(2011)37 cited
- → β-Sarcoglycan gene transfer decreases fibrosis and restores force in LGMD2E mice(2015)35 cited
- → Unmet Needs and Evolving Treatment for Limb Girdle Muscular Dystrophies(2021)34 cited
- → Gene therapy with bidridistrogene xeboparvovec for limb-girdle muscular dystrophy type 2E/R4: phase 1/2 trial results(2024)25 cited
- → Preclinical Systemic Delivery of Adeno-Associated α-Sarcoglycan Gene Transfer for Limb-Girdle Muscular Dystrophy(2020)22 cited