Francesca Simonelli
University of Campania "Luigi Vanvitelli"(IT)
Publications by Year
Research Areas
Retinal Development and Disorders, Retinal Diseases and Treatments, Retinal Imaging and Analysis, Glaucoma and retinal disorders, Retinal and Optic Conditions
Most-Cited Works
- → Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis(2008)2,126 cited
- → Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65 -mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial(2017)1,826 cited
- → Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial(2009)852 cited
- → Gene Therapy for Leber's Congenital Amaurosis is Safe and Effective Through 1.5 Years After Vector Administration(2009)551 cited
- → Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase 1 trial(2016)450 cited
- → AAV2 Gene Therapy Readministration in Three Adults with Congenital Blindness(2012)387 cited