Margaret V. Ragni
University of Pittsburgh(US)University of Pavia(IT)Azienda USL di Bologna(IT)Hemophilia Center of Western Pennsylvania(US)University of Pittsburgh Medical Center(US)Istituti di Ricovero e Cura a Carattere Scientifico(IT)
Publications by Year
Research Areas
Hemophilia Treatment and Research, Platelet Disorders and Treatments, Blood Coagulation and Thrombosis Mechanisms, Myeloproliferative Neoplasms: Diagnosis and Treatment, Blood groups and transfusion
Most-Cited Works
- → Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response(2006)2,115 cited
- → WFH Guidelines for the Management of Hemophilia, 3rd edition(2020)1,808 cited
- → Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector(2000)1,011 cited
- → AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B(2003)745 cited
- → Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant(2017)738 cited
- → CD8+ T-cell responses to adeno-associated virus capsid in humans(2007)720 cited