Leslie Nelson
United States Department of the Army(US)University of Buea(CM)Southwestern Medical Center(US)Children's Medical Center(US)Medical City Children's Hospital(US)The University of Texas Southwestern Medical Center(US)The University of Texas Southwestern Medical Center(US)
Publications by Year
Research Areas
Neurogenetic and Muscular Disorders Research, Muscle Physiology and Disorders, Cerebral Palsy and Movement Disorders, Congenital Anomalies and Fetal Surgery, Cardiomyopathy and Myosin Studies
Most-Cited Works
- → Diagnosis and management of spinal muscular atrophy: Part 1: Recommendations for diagnosis, rehabilitation, orthopedic and nutritional care(2017)1,011 cited
- → Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial(2017)451 cited
- → Consensus Statement on Standard of Care for Congenital Muscular Dystrophies(2010)212 cited
- → The gross motor function measure™ is a valid and sensitive outcome measure for spinal muscular atrophy(2006)89 cited
- → Rasch analysis of clinical outcome measures in spinal muscular atrophy(2013)77 cited
- → Evaluator Training and Reliability for SMA Global Nusinersen Trials(2018)54 cited