Dario Balestra
University of Ferrara(IT)
Publications by Year
Research Areas
Hemophilia Treatment and Research, RNA Research and Splicing, Neurogenetic and Muscular Disorders Research, RNA modifications and cancer, RNA Interference and Gene Delivery
Most-Cited Works
- → Mcl-1 involvement in mitochondrial dynamics is associated with apoptotic cell death(2015)128 cited
- → An exon-specific U1 small nuclear RNA (snRNA) strategy to correct splicing defects(2012)101 cited
- → U1-snRNA–mediated rescue of mRNA processing in severe factor VII deficiency(2007)58 cited
- → An engineered U1 small nuclear RNA rescues splicing‐defective coagulation F7 gene expression in mice(2013)47 cited
- → Molecular Basis and Therapeutic Strategies to Rescue Factor IX Variants That Affect Splicing and Protein Function(2016)42 cited
- → Regulation of a strongF9cryptic 5′ss by intrinsic elements and by combination of tailored U1snRNAs with antisense oligonucleotides(2015)29 cited
- → Rescue of coagulation factor VII function by the U1+5A snRNA(2009)29 cited
- → An Exon-Specific U1snRNA Induces a Robust Factor IX Activity in Mice Expressing Multiple Human FIX Splicing Mutants(2016)27 cited
- → Splicing Mutations Impairing CDKL5 Expression and Activity Can be Efficiently Rescued by U1snRNA-Based Therapy(2019)27 cited
- → Disease-causing variants of the conserved +2T of 5′ splice sites can be rescued by engineered U1snRNAs(2018)25 cited