Lindsay N. Alfano
Nationwide Children's Hospital(US)The Ohio State University Wexner Medical Center(US)The Ohio State University(US)
Publications by Year
Research Areas
Muscle Physiology and Disorders, Neurogenetic and Muscular Disorders Research, Cerebral Palsy and Movement Disorders, RNA modifications and cancer, Children's Physical and Motor Development
Most-Cited Works
- → Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy(2017)2,265 cited
- → Eteplirsen for the treatment of Duchenne muscular dystrophy(2013)778 cited
- → Longitudinal effect of eteplirsen versus historical control on ambulation in D uchenne muscular dystrophy(2015)497 cited
- → Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial(2017)451 cited
- → Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy(2020)377 cited
- → Five-Year Extension Results of the Phase 1 START Trial of Onasemnogene Abeparvovec in Spinal Muscular Atrophy(2021)263 cited