Alessandra Govoni
Azienda Ospedaliero-Universitaria Careggi(IT)
Publications by Year
Research Areas
Neurogenetic and Muscular Disorders Research, Muscle Physiology and Disorders, RNA modifications and cancer, Genetic Neurodegenerative Diseases, Congenital Anomalies and Fetal Surgery
Most-Cited Works
- → Improving Single Injection CSF Delivery of AAV9-mediated Gene Therapy for SMA: A Dose–response Study in Mice and Nonhuman Primates(2014)273 cited
- → Onasemnogene abeparvovec gene therapy for symptomatic infantile-onset spinal muscular atrophy type 1 (STR1VE-EU): an open-label, single-arm, multicentre, phase 3 trial(2021)241 cited
- → A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy(2014)229 cited
- → Nusinersen safety and effects on motor function in adult spinal muscular atrophy type 2 and 3(2020)189 cited
- → Genotype and phenotype characterization in a large dystrophinopathic cohort with extended follow-up(2011)188 cited
- → The italian limb girdle muscular dystrophy registry: Relative frequency, clinical features, and differential diagnosis(2016)123 cited
- → Safety and efficacy of olesoxime in patients with type 2 or non-ambulatory type 3 spinal muscular atrophy: a randomised, double-blind, placebo-controlled phase 2 trial(2017)114 cited
- → Discontinuation of Primary Prophylaxis forPneumocystis cariniiPneumonia and Toxoplasmic Encephalitis in Human Immunodeficiency Virus Type I–Infected Patients: The Changes in Opportunistic Prophylaxis Study(2000)108 cited
- → Cidofovir added to HAART improves virological and clinical outcome in AIDS-associated progressive multifocal leukoencephalopathy(2000)82 cited
- → Time Is Motor Neuron: Therapeutic Window and Its Correlation with Pathogenetic Mechanisms in Spinal Muscular Atrophy(2018)81 cited