Lyndsey Braun
Nationwide Children's Hospital(US)
Publications by Year
Research Areas
Neurogenetic and Muscular Disorders Research, Amyotrophic Lateral Sclerosis Research, RNA modifications and cancer, Neuroinflammation and Neurodegeneration Mechanisms, Thyroid Disorders and Treatments
Most-Cited Works
- → Single-Dose Gene-Replacement Therapy for Spinal Muscular Atrophy(2017)2,265 cited
- → Astrocytes from familial and sporadic ALS patients are toxic to motor neurons(2011)777 cited
- → RETRACTED ARTICLE: Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN(2010)689 cited
- → Microglia Induce Motor Neuron Death via the Classical NF-κB Pathway in Amyotrophic Lateral Sclerosis(2014)627 cited
- → Systemic Gene Delivery in Large Species for Targeting Spinal Cord, Brain, and Peripheral Tissues for Pediatric Disorders(2011)329 cited
- → Improving Single Injection CSF Delivery of AAV9-mediated Gene Therapy for SMA: A Dose–response Study in Mice and Nonhuman Primates(2014)273 cited
- → A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy(2014)229 cited
- → Early heart failure in the SMNΔ7 model of spinal muscular atrophy and correction by postnatal scAAV9-SMN delivery(2010)202 cited
- → Therapeutic AAV9-mediated Suppression of Mutant SOD1 Slows Disease Progression and Extends Survival in Models of Inherited ALS(2013)199 cited
- → Oligodendrocytes contribute to motor neuron death in ALS via SOD1-dependent mechanism(2016)180 cited