Matthew G. Woll
PTC Therapeutics (United States)(US)
Publications by Year
Research Areas
RNA Research and Splicing, RNA modifications and cancer, Neurogenetic and Muscular Disorders Research, Chemical Synthesis and Analysis, RNA and protein synthesis mechanisms
Most-Cited Works
- → SMN2 splicing modifiers improve motor function and longevity in mice with spinal muscular atrophy(2014)520 cited
- → Asymmetric Cooperative Catalysis of Strong Brønsted Acid–Promoted Reactions Using Chiral Ureas(2010)490 cited
- → Specific Correction of Alternative Survival Motor Neuron 2 Splicing by Small Molecules: Discovery of a Potential Novel Medicine To Treat Spinal Muscular Atrophy(2016)112 cited
- → Stabilizing and Destabilizing Effects of Phenylalanine → F5-Phenylalanine Mutations on the Folding of a Small Protein(2006)108 cited
- → Parallel Sheet Secondary Structure in γ-Peptides(2001)96 cited
- → Backbone Thioester Exchange: A New Approach to Evaluating Higher Order Structural Stability in Polypeptides(2004)87 cited
- → Small molecule splicing modifiers with systemic HTT-lowering activity(2021)85 cited
- → Stereoselective Synthesis of 3-Substituted 2-Aminocyclopentanecarboxylic Acid Derivatives and Their Incorporation into Short 12-Helical β-Peptides That Fold in Water(2002)62 cited
- → Discovery and Optimization of Small Molecule Splicing Modifiers of Survival Motor Neuron 2 as a Treatment for Spinal Muscular Atrophy(2016)61 cited
- → A deep learning approach to identify gene targets of a therapeutic for human splicing disorders(2021)47 cited