Azadeh Golipour
Publications by Year
Research Areas
CRISPR and Genetic Engineering, Pluripotent Stem Cells Research, Virus-based gene therapy research, RNA Research and Splicing, RNA Interference and Gene Delivery
Most-Cited Works
- → Functional Genomics Reveals a BMP-Driven Mesenchymal-to-Epithelial Transition in the Initiation of Somatic Cell Reprogramming(2010)1,001 cited
- → MBNL proteins repress ES-cell-specific alternative splicing and reprogramming(2013)346 cited
- → A Late Transition in Somatic Cell Reprogramming Requires Regulators Distinct from the Pluripotency Network(2012)152 cited
- → The Spy1/RINGO Family Represents a Novel Mechanism Regulating Mammary Growth and Tumorigenesis(2008)76 cited
- → Correction of pathology in mice displaying Gaucher disease type 1 by a clinically-applicable lentiviral vector(2020)23 cited
- → Looking into the Black Box: Insights into the Mechanisms of Somatic Cell Reprogramming(2011)8 cited
- → AVR-RD-01 lentiviral gene therapy reduces Gb3 substrate in endothelial cells of renal peritubular capillaries in a previously untreated classic Fabry disease male patient(2020)2 cited
- → The Guard1 clinical trial - A first in-human, phase 1/2 study evaluating AVR-RD-02, a hematopoietic stem cell (HSC) gene therapy for Gaucher disease: Preliminary safety, pharmacodynamic and clinical efficacy results from the subjects observed for up to 24 months post-infusion(2023)1 cited
- → Using IVIM/SAGA as screening tools during lentiviral vector lead selection for detection of clinically translatable insertional transformational risk(2023)1 cited
- → The GuardOne clinical trial: A first-in-human, open-label, multinational phase 1/2 study of AVR-RD-02 ex vivo lentiviral vector, autologous gene therapy for Gaucher disease(2021)1 cited