Juliet Lefferts
Utrecht University(NL)Pharmo Institute(NL)
Publications by Year
Research Areas
Cystic Fibrosis Research Advances, Neonatal Respiratory Health Research, Extracellular vesicles in disease, Tracheal and airway disorders, CRISPR and Genetic Engineering
Most-Cited Works
- → A CRISPR-Cas9-based reporter system for single-cell detection of extracellular vesicle-mediated functional transfer of RNA(2020)187 cited
- → Measuring cystic fibrosis drug responses in organoids derived from 2D differentiated nasal epithelia(2022)46 cited
- → Intestinal organoids for Cystic Fibrosis research(2019)45 cited
- → CFTR Function Restoration upon Elexacaftor/Tezacaftor/Ivacaftor Treatment in Patient-Derived Intestinal Organoids with Rare CFTR Genotypes(2023)33 cited
- → OrgaSegment: deep-learning based organoid segmentation to quantify CFTR dependent fluid secretion(2024)28 cited
- → Publisher Correction: A CRISPR-Cas9-based reporter system for single-cell detection of extracellular vesicle-mediated functional transfer of RNA(2020)10 cited
- → Elexacaftor/tezacaftor/ivacaftor efficacy in intestinal organoids with rare CFTR variants in comparison to CFTR-F508del and CFTR-wild type controls(2024)8 cited
- → A modular strategy for extracellular vesicle-mediated CRISPR-Cas9 delivery through aptamer-based loading and UV-activated cargo release(2024)7 cited
- → Targeted Locus Amplification and Haplotyping(2022)5 cited