Christian Mueller
Sanofi (France)(FR)AVEO Oncology (United States)(US)Sanofi (United States)(US)Center for Genomic Science(IT)
Publications by Year
Research Areas
Virus-based gene therapy research, RNA Interference and Gene Delivery, Viral Infectious Diseases and Gene Expression in Insects, Neurogenetic and Muscular Disorders Research, Amyotrophic Lateral Sclerosis Research
Most-Cited Works
- → Phase 2 Clinical Trial of a Recombinant Adeno-Associated Viral Vector Expressing α 1 -Antitrypsin: Interim Results(2011)323 cited
- → Sustained transgene expression despite T lymphocyte responses in a clinical trial of rAAV1-AAT gene therapy(2009)315 cited
- → Several rAAV Vectors Efficiently Cross the Blood–brain Barrier and Transduce Neurons and Astrocytes in the Neonatal Mouse Central Nervous System(2011)282 cited
- → Human C9ORF72 Hexanucleotide Expansion Reproduces RNA Foci and Dipeptide Repeat Proteins but Not Neurodegeneration in BAC Transgenic Mice(2015)255 cited
- → SOD1 Suppression with Adeno-Associated Virus and MicroRNA in Familial ALS(2020)241 cited
- → A divalent siRNA chemical scaffold for potent and sustained modulation of gene expression throughout the central nervous system(2019)221 cited