Scott McPhee
UK Astronomy Technology Centre(GB)
Publications by Year
Research Areas
Virus-based gene therapy research, Viral Infectious Diseases and Gene Expression in Insects, CAR-T cell therapy research, Viral Infections and Immunology Research, Advanced MRI Techniques and Applications
Most-Cited Works
- → Dystrophin Immunity in Duchenne's Muscular Dystrophy(2010)651 cited
- → Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector(2011)390 cited
- → Long-Term Follow-Up After Gene Therapy for Canavan Disease(2012)323 cited
- → Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle(2009)255 cited
- → Gene Therapy of Canavan Disease: AAV-2 Vector for Neurosurgical Delivery of Aspartoacylase Gene ( ASPA ) to the Human Brain(2002)251 cited
- → Immune responses to AAV in a phase I study for Canavan disease(2006)236 cited
- → BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression(2020)183 cited
- → Aspartoacylase gene transfer to the mammalian central nervous system with therapeutic implications for Canavan disease(2000)177 cited
- → Employing a Gain-of-Function Factor IX Variant R338L to Advance the Efficacy and Safety of Hemophilia B Human Gene Therapy: Preclinical Evaluation Supporting an Ongoing Adeno-Associated Virus Clinical Trial(2014)107 cited
- → Cardiac I-1c Overexpression With Reengineered AAV Improves Cardiac Function in Swine Ischemic Heart Failure(2014)83 cited